Rescuing protein conformation: prospects for pharmacological therapy in cystic fibrosis

J Clin Invest. 2002 Dec;110(11):1591-7. doi: 10.1172/JCI16786.
No abstract available

Publication types

  • Review

MeSH terms

  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / genetics
  • Cystic Fibrosis Transmembrane Conductance Regulator / chemistry
  • Cystic Fibrosis Transmembrane Conductance Regulator / genetics*
  • Gene Expression Regulation
  • Humans
  • Molecular Chaperones / physiology
  • Mutation*
  • Protein Conformation*

Substances

  • CFTR protein, human
  • Molecular Chaperones
  • Cystic Fibrosis Transmembrane Conductance Regulator