Discovery of a phosphodiesterase 9A inhibitor as a potential hypoglycemic agent

J Med Chem. 2014 Dec 26;57(24):10304-13. doi: 10.1021/jm500836h. Epub 2014 Dec 8.

Abstract

Phosphodiesterase 9 (PDE9) inhibitors have been studied as potential therapeutics for treatment of diabetes and Alzheimer's disease. Here we report a potent PDE9 inhibitor 3r that has an IC50 of 0.6 nM and >150-fold selectivity over other PDEs. The HepG2 cell-based assay shows that 3r inhibits the mRNA expression of phosphoenolpyruvate carboxykinase and glucose 6-phosphatase. These activities of 3r, together with the reasonable pharmacokinetic properties and no acute toxicity at 1200 mg/kg dosage, suggest its potential as a hypoglycemic agent. The crystal structure of PDE9-3r reveals significantly different conformation and hydrogen bonding pattern of 3r from those of previously published 28s. Both 3r and 28s form a hydrogen bond with Tyr424, a unique PDE9 residue (except for PDE8), but 3r shows an additional hydrogen bond with Ala452. This structure information might be useful for design of PDE9 inhibitors.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • 3',5'-Cyclic-AMP Phosphodiesterases / antagonists & inhibitors*
  • Animals
  • Blotting, Western
  • Body Fluids / chemistry
  • Catalytic Domain
  • Crystallography, X-Ray
  • Drug Discovery
  • Gene Expression Regulation, Neoplastic / drug effects*
  • Glucose-6-Phosphatase / antagonists & inhibitors*
  • Hep G2 Cells
  • Humans
  • Hydrogen Bonding
  • Hypoglycemic Agents / chemistry
  • Hypoglycemic Agents / pharmacokinetics
  • Hypoglycemic Agents / pharmacology*
  • Mice
  • Microsomes, Liver / drug effects*
  • Microsomes, Liver / metabolism
  • Models, Molecular
  • Molecular Structure
  • Phosphodiesterase Inhibitors / chemistry
  • Phosphodiesterase Inhibitors / pharmacokinetics
  • Phosphodiesterase Inhibitors / pharmacology*
  • Protein Serine-Threonine Kinases / antagonists & inhibitors*
  • Pyrazoles / chemistry
  • Pyrazoles / pharmacokinetics
  • Pyrazoles / pharmacology*
  • Pyrimidinones / chemistry
  • Pyrimidinones / pharmacokinetics
  • Pyrimidinones / pharmacology*
  • RNA, Messenger / genetics
  • Real-Time Polymerase Chain Reaction
  • Reverse Transcriptase Polymerase Chain Reaction
  • Structure-Activity Relationship
  • Tissue Distribution

Substances

  • 2-((1-cyclopentyl-4-hydroxy-1H-pyrazolo(3,4-d)pyrimidin-6-yl)amino)-N-(4-methoxyphenyl)propanamide
  • Hypoglycemic Agents
  • Phosphodiesterase Inhibitors
  • Pyrazoles
  • Pyrimidinones
  • RNA, Messenger
  • phosphoenolpyruvate carboxylase kinase
  • Protein Serine-Threonine Kinases
  • Glucose-6-Phosphatase
  • 3',5'-Cyclic-AMP Phosphodiesterases
  • PDE9A protein, human

Associated data

  • PDB/4QGE